U.S. Food and Drug Administration Approves CRESTOR(R) for Use in Pediatric Patients With Heterozygous Familial Hypercholesterole
16 Outubro 2009 - 9:00AM
PR Newswire (US)
WILMINGTON, Del., Oct. 16 /PRNewswire-FirstCall/ -- AstraZeneca
(NYSE: AZN) today announced the U.S. Food and Drug Administration
(FDA) approved CRESTOR® (rosuvastatin calcium) for use in pediatric
patients ages 10-17 with heterozygous familial hypercholesterolemia
(HeFH) when diet therapy fails to reduce elevated cholesterol.
HeFH, a genetic disease, is characterized by high LDL cholesterol
(the "bad" cholesterol) and increased risk of early cardiovascular
disease. The FDA decision was based on a supplemental New Drug
Application submitted by AstraZeneca which included data from the
PLUTO (Pediatric Lipid-redUction Trial of rOsuvastatin) study.
PLUTO was designed to evaluate the efficacy and safety of CRESTOR
in children ages 10-17 with HeFH. "AstraZeneca is committed to
studying the impact of CRESTOR in various populations with a high
unmet medical need, including pediatric and adolescent patients.
Information about the effects of CRESTOR in pediatric patients with
HeFH will now be included in the CRESTOR Prescribing Information,"
said Alex Gold, MD, Executive Director of Clinical Development for
CRESTOR, AstraZeneca US. "While we believe it was important to
investigate the use of CRESTOR in these patients, AstraZeneca does
not plan to actively promote this indication." In July, AstraZeneca
announced the FDA had granted an additional six-month period of
exclusivity to market CRESTOR® (rosuvastatin calcium) for its
approved cholesterol and atherosclerosis indications until July
2016. The decision was based on the supplemental New Drug
Application submitted by AstraZeneca. The completion of the PLUTO
study satisfied AstraZeneca's commitment to the FDA to conduct a
study evaluating the impact of CRESTOR on this pediatric
population. About Heterozygous Familial Hypercholesterolemia
Heterozygous familial hypercholesterolemia affects 10 million
people worldwide(1) and is most commonly caused by a defect in the
LDL-C receptor gene that leads to elevated LDL-C levels. The
American Academy of Pediatrics states that pharmacological
intervention should be considered for children with LDL levels
greater than 190 mg/dL. About PLUTO The PLUTO (Pediatric
Lipid-redUction Trial of rOsuvastatin) study was a 12-week,
double-blind, randomized multicenter, placebo-controlled study with
a 40-week, open-label follow-up. The PLUTO study was designed to
evaluate the efficacy and safety of CRESTOR in children ages 10-17
with heterozygous familial hypercholesterolemia (HeFH), a genetic
disease characterized by high LDL cholesterol (the "bad"
cholesterol) and early cardiovascular disease. About CRESTOR
(rosuvastatin calcium): Studies have previously shown that CRESTOR,
as an adjunct to diet in adult patients, significantly lowered
LDL-C, had a significant effect on raising HDL-C and slowed the
progression of atherosclerosis, an underlying cause of
cardiovascular disease. CRESTOR is indicated as an adjunct to diet
to reduce elevated Total-C, LDL-C, ApoB, non-HDL-C, and TG levels
and to increase HDL-C in patients with primary hyperlipidemia and
mixed dyslipidemia. CRESTOR is also approved for pediatric patients
10 to 17 years of age with heterozygous familial
hypercholesterolemia (HeFH) after failing an adequate trail of diet
therapy. CRESTOR is also indicated as an adjunct to diet to slow
the progression of atherosclerosis in adult patients as part of a
treatment strategy to lower Total-C and LDL-C to target levels.
CRESTOR is not approved to reduce cardiovascular morbidity and
mortality. CRESTOR has now received regulatory approval in over 95
countries. Nearly 17 million patients have been prescribed CRESTOR
worldwide. Data from clinical trials and real world use shows that
the safety profile for CRESTOR is in line with other marketed
statins. Important Safety Information: CRESTOR is contraindicated
in patients with a known hypersensitivity to any component of this
product, in patients with active liver disease, which may include
unexplained persistent elevations of hepatic transaminase levels,
in women who are pregnant or may become pregnant, and in nursing
mothers. Cases of myopathy and rhabdomyolysis with acute renal
failure secondary to myoglobinuria have been reported with HMG-CoA
reductase inhibitors, including CRESTOR. These risks can occur at
any dose level, but are increased at the highest dose (40 mg).
CRESTOR should be prescribed with caution in patients with
predisposing factors for myopathy (eg, age greater than or equal to
65 years, inadequately treated hypothyroidism, renal impairment).
The risk of myopathy during treatment with CRESTOR may be increased
with concurrent administration of some other lipid-lowering
therapies (fibrates or niacin), gemfibrozil, cyclosporine, or
lopinavir/ritonavir. Therapy with CRESTOR should be discontinued if
markedly elevated CK levels occur or myopathy is diagnosed or
suspected. All patients should be advised to promptly report
unexplained muscle pain, tenderness, or weakness, particularly if
accompanied by malaise or fever. It is recommended that liver
enzyme tests be performed before and at 12 weeks following both the
initiation of therapy and any elevation of dose, and periodically
(e.g., semiannually) thereafter. Should an increase in ALT or AST
of >3 times ULN persist, reduction of dose or withdrawal of
CRESTOR is recommended. CRESTOR should be used with caution in
patients who consume substantial quantities of alcohol. CRESTOR 40
mg should be used only for those patients not achieving their LDL-C
goal with 20 mg. Patients initiating CRESTOR therapy or switching
from another statin should begin treatment with CRESTOR at the
appropriate starting dose. In the controlled clinical trials
database, the most common adverse reactions were headache (3.7%),
myalgia (3.1%), abdominal pain (2.6%), asthenia (2.5%), and nausea
(2.2%). Please see accompanying full Prescribing Information. If
you have any questions concerning CRESTOR, please contact
AstraZeneca at 1-800-237-8898. CRESTOR is a registered trademark of
the AstraZeneca group of companies. About AstraZeneca AstraZeneca
is engaged in the research, development, manufacturing and
marketing of meaningful prescription medicines and in the supply of
healthcare services. AstraZeneca is one of the world's leading
pharmaceutical companies with global healthcare sales of $ 31.6
billion and is a leader in gastrointestinal, cardiovascular,
neuroscience, respiratory, oncology and infectious disease
medicines. In the United States, AstraZeneca is a $13.5 billion
dollar healthcare business. For more information about AstraZeneca
in the US or our AZ&Me(TM) Prescription Savings programs,
please visit: http://www.astrazeneca-us.com/. (1) Marks D et al.
Atherosclerosis 2003; 168: 1-14 DATASOURCE: AstraZeneca CONTACT:
Media Inquiries: Rhea Lewis, +1-302-885-4614, Donna Huang,
+1-302-885-6396, Investor Inquiries US: Ed Seage, +1-302-886-4065,
Cell, +1-302-373-1361, Jorgen Winroth, +1-212-579-0506, Cell,
+1-917-612-4043 Web Site: http://www.astrazeneca-us.com/
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